• Effects of Trehalose Administration in Patients with Mucopolysaccharidosis Type III 

      Mobini, Moein; Radbakhsh, Shabnam; Kubaski, Francyne; Eshraghi, Peyman; Vakili, Saba; ... more authors ( Bentham Science Publishers , 2023 , Article)
      Background and Aim: Mucopolysaccharidosis type III (MPS III) is a rare autosomal recessive lysosomal storage disease (LSD) caused by a deficiency of lysosomal enzymes required for the catabolism of glycosaminoglycans (GAGs), ...