Browsing Public Health by Subject "Antisense oligonucleotide"

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    • Tofersen for SOD1 amyotrophic lateral sclerosis: a systematic review and meta-analysis 

      Hamad, Abdullah Ashraf; Alkhawaldeh, Ibraheem M.; Nashwan, Abdulqadir J.; Meshref, Mostafa; Imam, Yahia ( Springer-Verlag Italia s.r.l. , 2025 , Article Review)
      Objective: Tofersen, an antisense oligonucleotide, has recently received FDA and EMA approval for treating amyotrophic lateral sclerosis (ALS) in adults with SOD1 gene mutations. This systematic review and meta-analysis ...