Browsing Medicine Research by Author "Radbakhsh, Shabnam"
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Effects of Trehalose Administration in Patients with Mucopolysaccharidosis Type III.
Mobini, Moein; Radbakhsh, Shabnam; Kubaski, Francyne; Eshraghi, Peyman; Vakili, Saba; Vakili, Rahim; Abbasifard, Mitra; Jamialahmadi, Tannaz; Rajabi, Omid; Emami, Seyed Ahmad; Tayarani-Najaran, Zahra; Rizzo, Manfredi; Eid, Ali H; Banach, Maciej; Sahebkar, Amirhossein... more authors ... less authors ( Europe PMC , 2023 , Article)Mucopolysaccharidosis type III (MPS III) is a rare autosomal recessive lysosomal storage disease (LSD) caused by a deficiency of lysosomal enzymes required for the catabolism of glycosaminoglycans (GAGs), mainly in the ...